FDA probes tumour risk tied to Novartis gene therapy

ZURICH, Nov 6 (Reuters) - The US Food and Drug Administration said on Friday it was investigating a risk of neoplasia, or ...

Novartis reveals cancer cases possibly linked to gene therapy Zolgensma

The occurrence of cancer in nine recipients — two of which involved evidence that a viral delivery tool integrated into ...

Novartis Says Tumors Found in Children Given SMA Gene Therapy

Children taking Novartis’s Zolgensma gene therapy for the deadly condition of spinal muscular atrophy have developed tumors, ...

As a baby I lived in a protective 'bubble' but after pioneering gene therapy I beat Covid twice

Rhys faced spending his life in isolation from the world but now works as stage crew at Butlin's.
BioSpace

Forge’s Piteri-Molina on AI, Ohio and what’s next for gene therapy manufacturing

The BioSpace 40 Under 40 honoree helped steer Forge’s sale to Ajinomoto. Now, Samantha Piteri-Molina sees opportunities in AI ...

Crigler-Najjar syndrome: Gene therapy maintains its efficacy four years after treatment

The New England Journal of Medicine has published a study on the long-term efficacy of AAV8-mediated gene therapy (GNT0003) ...
RTTNews

FDA Investigates Cancer Risk Associated With Novartis' Zolgensma Gene Therapy

The FDA has determined that the risk of neoplasia, including malignancy, applies to both Zolgensma and Itvisma, as they ...
Nature

Epileptic seizures nearly vanish after people receive experimental gene therapy in their brains

Three people with epilepsy resistant to drug treatment saw the number of seizures they had per month fall by more than 90%, ...

Epilepsy breakthrough: Experimental gene therapy cuts seizures by over 90% in first human trial

Unlike conventional epilepsy treatments, which generally rely on medicines to suppress seizures across the brain, this ...
GEN - Genetic Engineering and Biotechnology News

Novartis Confirms Nine Cases of Tumors in Children Treated with Gene Therapy Zolgensma

Novartis has confirmed nine instances—seven of them newly disclosed—in which tumors have developed in children treated with ...
Nature

Gene therapy that led to boy’s death had limited efficacy

Therapy pioneered by biotechnology Chinese firm HuidaGene showed promise in animals but caused a fatal reaction in a child.

Global Hemophilia B Gene Therapy Market Report 2026 | Capitalize on 29.8% CAGR as Pfizer, CSL Behring, Bayer, and REGENXBIO Accelerate AAV Innovation

Boost ROI via optimized AAV platforms, personalized dosing, expanded trials and patient access, and localized vector production to cut tariff costs and accelerate commercialization.Dublin, Nov. 06, ...