Exclusive: One in four wait at least three years for diagnosis and many face treatment ‘access lottery’, according to report ...
In India, rare diseases are not so rare. It is estimated that around 70 million Indians live with one of more than 7,000 rare ...
Explore why patient engagement is the cornerstone of successful rare disease trials, emphasising the importance of designing studies around the realities of patients' lives to build trust and improve ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results