First evidence of a 'critical priority' fungal pathogen becoming more deadly when co-infected with tuberculosis

Cryptococcus neoformans is one of four fungi classified as "critical priority" on the WHO's Fungal Pathogens Priority List, ...

FDA proposes new system for approving customized drugs and therapies for rare diseases

The Food and Drug Administration is proposing a system for approving customized drugs and medical treatments for patients with rare or hard-to-treat diseases.

The hidden infections that refuse to go away: How household practices can stop deadly diseases

A 13-year study led by the Colorado School of Public Health at the University of Colorado Anschutz reveals why a deadly ...

FDA proposes new treatment approval pathway for ultrarare diseases

The Food and Drug Administration (FDA) announced a new proposal Monday for flexible drug approval pathway treatments ...

US FDA proposes framework to speed rare disease gene therapy approvals

WASHINGTON, Feb 23 (Reuters) - The U.S. Food and Drug Administration proposed on Monday a new framework to speed approvals of ...
Opinion

FDA: How We’re Approving More Drugs to Treat Rare Diseases

Our application process was designed for common ailments, but roughly 30 million Americans suffer from uncommon ones.
Healio

Q&A: Researchers create system to engineer synthetic phages

Researchers from New England Biolabs and Yale University have created a system for engineering the first fully synthetic ...

Is Early Detection Of Rare Diseases Hidden In Your Genes?

In many countries, newborn screening programmes test babies for certain inherited conditions shortly after birth.
BioSpace

FDA’s Bespoke Pathway To Focus on Gene Editing and RNA-Based Treatments for Rare Diseases

The framework, first introduced by FDA Commissioner Marty Makary and Center for Biologics Evaluation and Research head Vinay ...
Science Daily

Scientists create universal nasal spray vaccine that protects against COVID, flu, and pneumonia

Scientists at Stanford Medicine have unveiled a bold new kind of “universal” vaccine that could one day protect against everything from COVID-19 and the flu to bacterial pneumonia and even common ...
KUOW

The FDA creates a quicker path for gene therapies

The Food and Drug Administration aims to evaluate treatments for rare diseases based on plausible evidence that they would ...