Myotonic dystrophy type 1 is a rare, dominantly inherited, progressive, disabling, neuromuscular disease that leads to decreased life expectancy and has no approved therapies. The disease is caused by ...

Momentum Over Milestones: Success is not the destination you applaud at the finish line; it is the courage to stay aboard while the landscape blurs, the turns tighten, and the goalpost keeps moving ...

A gene therapy for Duchenne muscular dystrophy caused complications to the liver, prompting a review of its use for younger patients. By Christina Jewett The Food and Drug Administration said on ...

FRANKFURT, Nov 4 (Reuters) - Germany's Reflex Aerospace, which makes satellites for civil and defence use, on Tuesday said it had closed a 50 million euro ($58.3 million) Series A funding round to ...

Jason is a general assignment reporter, with particular focus on genetic medicine and rare disease. Confidential tips can be sent on Signal at JasonMast.77. BridgeBio said Monday that an experimental ...

Harry Nugraha is a contributor from Indonesia. He is an anime addict first and a freelance writer second. He's been writing about anime and manga since 2020, and he loves to watch an unhealthy amount ...

Price: How much does it cost? Are there payment plans available? Including customizations, taxes, and a $279 flat-rate fee for in-home delivery and assembly, the total price came to $3,576. The base ...

** When you buy products through the links on our site, we may earn a commission that supports NRA's mission to protect, preserve and defend the Second Amendment. ** We first saw the FN Reflex in 2023 ...

Christine McSherry is a registered nurse and founder of Jett Foundation. On Sunday at 1 a.m. Eastern time, an announcement went out from the first-generation gene therapy company for Duchenne muscular ...

Scientists present current evidence for a new gene therapy for Duchenne muscular dystrophy called delandistrogene moxeparvovec. AAN Evidence in Focus articles highlight the strength of the current ...

The sympathetic nervous system, which helps your heart and other vital organs function all the time, increases activity in response to danger or stress, preparing the body for extra demands. Stress is ...

Over the past year, there’s one athleisure item I’ve spotted in just about every workout class I’ve been to: Lululemon’s Define jacket. Because we review the cult-favorite workout brand regularly here ...