For the first time, researchers revealed the structures underlying a family of debilitating genetic disorders Using advanced instrumentation and methods, the scientists were able to witness how ...

Former Titans running back and NFL legend Chris Johnson has announced he has ALS, nearly a decade after retiring from the ...

A Novartis RNA therapy reduced blood levels of a protein that’s a biological indicator of a particular form of muscular dystrophy, clinical trial results that could support an application seeking a ...

University of Maine researchers have published new findings about how muscles form, why certain muscle diseases develop and why symptoms may not appear until years after muscle degeneration begins.

May 14 (Reuters) - Regenxbio said on Thursday that its experimental gene therapy for a muscle-wasting disorder met the main goal in a late-stage study, but its shares plunged 31% in morning trading ...

Myofibrillar myopathy type 6 (MFM6) is a rare genetic muscle disorder that leads to severe muscle weakness and a drastically shortened life expectancy due to a disruption in muscle protein regulation.

Myofibrillar myopathy type 6 (MFM6) is a rare genetic muscle disorder that leads to severe muscle weakness and a drastically shortened life expectancy due to a disruption in muscle protein regulation.

Under the terms of the companies’ previous agreement, Dyno will receive a $15 million fee, along with potential milestone and royalty payments. (iStock/Getty Images Plus) Under a research ...

PepGen (PEPG) shares fell ~44% in after-hours trading after the Massachusetts-based biotech company shared results from a mid-stage trial for its main treatment, PGN-EDODM1, which is aimed at myotonic ...

PepGen shares fell after the company shared mixed results for its muscle-disorder treatment. The stock slid 48% to $2.20 in after-hours trading Monday. Shares are down 35% this year. PepGen shared ...

Chugai Pharmaceutical Co. fell 7.3%, the largest intraday decline since August 2025, after the company said it had ended the development of an experimental drug for certain diseases that cause muscle ...

Facioscapulohumeral muscular dystrophy (Facio-face; scapulo-scapula or shoulder blade; humeral-arm muscles around the humerus) or FSHD is an inherited muscle disorder characterized by the progressive ...